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\u4f8b SMA \u60a3\u8005<sup>[2]<\/sup>\uff1b\u7ea680%\u7684\u60a3\u8005\u4f1a\u5728\u51fa\u751f\u540e 18 \u4e2a\u6708\u5185\u8d77\u75c5<sup>[3]<\/sup>\uff0c\u75c5\u60c5\u7684\u8fdb\u5c55\u53ef\u5bfc\u81f4\u5168\u8eab\u591a\u7cfb\u7edf\u5f02\u5e38\u3002\u91cd\u75c7SMA\u60a3\u513f\u5982\u4e0d\u8fdb\u884c\u6709\u6548\u6cbb\u7597\uff0c\u591a\u6570\u4f1a\u57282\u5c81\u5185\u592d\u6298<sup>[4]<\/sup>\u3002<\/p>\n<p>\u7531\u4e8e\u793e\u4f1a\u5bf9\u75be\u75c5\u6574\u4f53\u8ba4\u77e5\u7684\u7f3a\u4e4f\uff0cSMA\u60a3\u8005\u4e0e\u5bb6\u5ead\u4e00\u76f4\u4ee5\u6765\u9762\u4e34\u7740\u786e\u8bca\u96be\u3001\u786e\u8bca\u65f6\u95f4\u957f\u7684\u95ee\u9898\uff1b\u52a0\u4e4b\u7f55\u89c1\u75c5\u836f\u7269\u7684\u4f7f\u7528\u8005\u5c11\u3001\u7814\u53d1\u6210\u672c\u9ad8\u3001\u96be\u5ea6\u5927\uff0c\u6cbb\u7597\u65b9\u5f0f\u6781\u4e3a\u6709\u9650\u3001\u53ef\u652f\u4ed8\u6027\u4f4e\u7684\u56f0\u5883\u4e5f\u957f\u671f\u5b58\u5728\u3002\u56e0\u6b64\uff0c\u66f4\u591a\u7597\u6548\u786e\u5207\u3001\u4f7f\u7528\u4fbf\u5229\u7684\u836f\u7269\u80fd\u591f\u88ab\u7eb3\u5165\u533b\u4fdd\u662f\u8bb8\u591aSMA\u60a3\u8005\u53ca\u5bb6\u5ead\u7684\u8feb\u5207\u613f\u671b\u3002<\/p>\n<p>\u6b64\u5916\uff0c\u540c\u5927\u591a\u6570\u7f55\u89c1\u75c5\u7fa4\u4f53\u4e00\u6837\uff0c\u8bb8\u591aSMA\u5bb6\u5ead\u4e5f\u957f\u671f\u53d7\u5230\u7167\u62a4\u538b\u529b\u6c89\u91cd\u3001\u96be\u4ee5\u6b63\u5e38\u878d\u5165\u793e\u4f1a\u7b49\u8bf8\u591a\u73b0\u5b9e\u96be\u9898\u56f0\u6270\uff0c\u4e9f\u9700\u66f4\u5168\u9762\u7684\u793e\u4f1a\u4fdd\u969c\u4f53\u7cfb\u7684\u652f\u6301\u3002<\/p>\n<p><b>\u53e3\u670d\u836f\u7269\u4f18\u52bf\u51f8\u663e\uff0c\u533b\u4fdd\u52a9\u63a8\u521b\u65b0\u53ef\u53ca<\/b><\/p>\n<p>\u81ea2020\u5e748\u6708\u83b7\u5f97\u7f8e\u56fdFDA\u6279\u51c6\u4ee5\u6765\uff0c\u827e\u6ee1\u6b23<sup>&reg;<\/sup>\u76ee\u524d\u5df2\u5728\u5168\u7403\u8d85\u8fc780\u4e2a\u56fd\u5bb6\u83b7\u6279\uff0c\u6570\u5343\u540d\u60a3\u8005\u5728\u771f\u5b9e\u4e16\u754c\u4e2d\u63a5\u53d7\u4e86\u827e\u6ee1\u6b23<sup>&reg;<\/sup>\u7684\u6cbb\u7597\uff0c\u5176\u6709\u6548\u6027\u53ca\u5b89\u5168\u6027\u5f97\u5230\u5e7f\u6cdb\u8bc1\u5b9e\u3002\u4f5c\u4e3a\u9996\u4e2a\u9776\u5411mRNA\u7684\u5c0f\u5206\u5b50\u75be\u75c5\u4fee\u6b63\u6cbb\u7597\u836f\u7269\uff0c\u5b83\u53ef\u7a7f\u900f\u8840\u8111\u5c4f\u969c\uff0c\u5206\u5e03\u4e8e\u4e2d\u67a2\u548c\u5916\u5468\u7ec4\u7ec7\uff0c\u5168\u8eab\u6027\u589e\u52a0SMN\u86cb\u767d\u6c34\u5e73\u3002\u7814\u7a76\u7ed3\u679c\u663e\u793a\uff0c\u827e\u6ee1\u6b23<sup>&reg;<\/sup>\u6cbb\u7597\u540e\u76841\u578bSMA\u60a3\u8005\u751f\u5b58\u7387\u8f83\u4e4b\u81ea\u7136\u53f2\u663e\u8457\u63d0\u9ad8\uff0c\u5b9e\u73b0\u8fd0\u52a8\u91cc\u7a0b\u7891\uff0c\u547c\u5438\u548c\u541e\u54bd\u529f\u80fd\u83b7\u5f97\u6539\u5584<sup>[5]<\/sup>\uff1b2\u578b\u548c3\u578bSMA\u60a3\u8005\u7528\u836f\u540e\u8fd0\u52a8\u529f\u80fd\u53ca\u751f\u6d3b\u72ec\u7acb\u6027\u83b7\u5f97\u6539\u5584\u3002<\/p>\n<p>\u5176\u7a81\u7834\u6027\u7684\u53e3\u670d\u7ed9\u836f\u65b9\u5f0f\uff0c\u4f7f\u5f97\u60a3\u8005\u53ef\u8fdb\u884c\u5c45\u5bb6\u6cbb\u7597\uff0c\u65e0\u9700\u4f4f\u9662\u3001\u63a5\u53d7\u4fb5\u5165\u6027\u624b\u672f\u6216\u540c\u65f6\u4f7f\u7528\u5176\u5b83\u836f\u7269\uff0c\u8fd9\u4e0d\u4ec5\u63d0\u9ad8\u4e86\u60a3\u8005\u7528\u836f\u7684\u4f9d\u4ece\u6027\uff0c\u4e5f\u51cf\u8f7b\u4e86\u533b\u9662\u7684\u516c\u5171\u533b\u7597\u8d44\u6e90\u538b\u529b\u3002\u540c\u65f6\uff0c\u827e\u6ee1\u6b23<sup>&reg;<\/sup>\u9636\u68af\u5242\u91cf\u7ed9\u836f\u7684\u4f7f\u7528\u65b9\u5f0f\u8fdb\u4e00\u6b65\u51cf\u5c11\u4e86\u4f4e\u9f84\u60a3\u8005\u7684\u7528\u836f\u8d1f\u62c5\uff0c\u6709\u52a9\u4e8e\u63a8\u52a8\u5c3d\u65e9\u6cbb\u7597\u3002<\/p>\n<p>&quot;\u5229\u53f8\u6251\u5170\u5c06\u6211\u56fdSMA\u6cbb\u7597\u5e26\u5165\u4e86\u2018\u53e3\u670d\u65f6\u4ee3&#8217;\uff0c\u5176\u8fdb\u5165\u56fd\u5bb6\u533b\u4fdd\u76ee\u5f55\u5c06\u5927\u5927\u63d0\u9ad8\u521b\u65b0\u7597\u6cd5\u7684\u53ef\u53ca\u6027\uff0c\u51cf\u8f7b\u60a3\u8005\u4e0e\u5176\u5bb6\u5ead\u7684\u8d1f\u62c5\uff0c\u4e3a\u73b0\u6709\u7684\u4e34\u5e8a\u6cbb\u7597\u65b9\u6848\u63d0\u4f9b\u4e86\u91cd\u8981\u8865\u5145\uff0c\u5f25\u8865\u4e86\u73b0\u6709\u76ee\u5f55\u5185\u836f\u7269\u7684\u5c40\u9650\u6027\uff0c\u5c24\u5176\u5bf9\u957f\u671f\u9762\u4e34\u2018\u7f3a\u533b\u5c11\u836f&#8217;\u56f0\u5883\u7684\u8bb8\u591aSMA\u5bb6\u5ead\u6765\u8bf4\uff0c\u521b\u65b0\u836f\u7269\u7684\u53ef\u53ca\u4e5f\u610f\u5473\u7740\u2018\u751f\u547d\u5e0c\u671b&#8217;\u7684\u53ef\u53ca\u3002&quot;\u590d\u65e6\u5927\u5b66\u9644\u5c5e\u513f\u79d1\u533b\u9662\u738b\u827a\u6559\u6388\u8868\u793a\uff0c&quot;\u4ece\u957f\u8fdc\u6765\u770b\uff0c\u8fd9\u4e5f\u5c06\u5e26\u52a8\u4e2d\u56fdSMA\u6574\u4f53\u8bca\u7597\u6c34\u5e73\u548c\u5168\u75c5\u7a0b\u7ba1\u7406\u7684\u53d1\u5c55\u4e0e\u5b8c\u5584\u3002&quot;<\/p>\n<p>&quot;SMA\u662f\u4e00\u4e2a\u9700\u8981\u7ec8\u8eab\u6cbb\u7597\u7684\u75be\u75c5\uff0c\u5176\u957f\u671f\u6cbb\u7597\u8d1f\u62c5\u4e00\u76f4\u662f\u5404\u65b9\u5173\u6ce8\u7684\u7126\u70b9\u3002\u4f5c\u4e3a\u60a3\u8005\u5173\u7231\u7ec4\u7ec7\uff0c\u6211\u4eec\u966a\u4f34\u60a3\u8005\u5bb6\u5ead\u7ecf\u5386\u8fc7\u8bb8\u591a\u66f2\u6298\u4e0e\u65e0\u5948\u7684\u65f6\u523b\uff0c\u4e5f\u56e0\u6b64\u5bf9\u53e3\u670d\u521b\u65b0\u836f\u7269\u8fdb\u5165\u533b\u4fdd\u611f\u5230\u683c\u5916\u632f\u594b\u3002\u6cbb\u7597\u53ef\u53ca\u6027\u7684\u4e0d\u65ad\u63d0\u9ad8\uff0c\u5c06\u66f4\u52a0\u6709\u529b\u5730\u652f\u6301\u6211\u4eec\u8df5\u884c\u2018\u5e2e\u52a9\u75c5\u60a3\u5bb6\u5ead\u66f4\u6709\u5e0c\u671b\u548c\u5c0a\u4e25\u5730\u9762\u5bf9\u75be\u75c5&#8217;\u8fd9\u4e00\u4f7f\u547d\u3002&quot;\u7f8e\u513fSMA\u5173\u7231\u4e2d\u5fc3\u6267\u884c\u603b\u76d1\u90a2\u7115\u840d\u8c08\u5230\u3002<\/p>\n<p><b>\u653f\u7b56\u53d1\u529b\u7f55\u89c1\u75c5\u9632\u6cbb\uff0c\u653f\u4f01\u643a\u624b\u52a0\u901f\u4fdd\u969c\u5b8c\u5584<\/b><\/p>\n<p>2018\u5e74\uff0c\u56fd\u5bb6\u536b\u5065\u59d4\u7b495\u90e8\u95e8\u8054\u5408\u5236\u5b9a\u5305\u62ecSMA\u5728\u5185\u7684\u300a\u7b2c\u4e00\u6279\u7f55\u89c1\u75c5\u76ee\u5f55\u300b\uff0c\u300a\u7f55\u89c1\u75c5\u8bca\u7597\u6307\u5357\uff082019\u5e74\u7248\uff09\u300b\u4e5f\u4e8e\u6b21\u5e74\u53d1\u5e03\uff1b\u56fd\u5bb6\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40\u8fde\u7eed\u51fa\u53f0\u4e86\u4e09\u6279\u300a\u4e34\u5e8a\u6025\u9700\u5883\u5916\u65b0\u836f\u540d\u5355\u300b\uff0c\u8fde\u540c\u4f18\u5148\u5ba1\u8bc4\u5ba1\u6279\u653f\u7b56\uff0c\u52a0\u901f\u7f55\u89c1\u75c5\u836f\u54c1\u5728\u6211\u56fd\u4e0a\u5e02\u8fdb\u5ea6\u3002\u8fd9\u4e00\u7cfb\u5217\u4e3e\u63aa\uff0c\u4f53\u73b0\u4e86\u56fd\u5bb6\u5bf9\u7f55\u89c1\u75c5\u7fa4\u4f53\u7684\u91cd\u89c6\uff0c\u4ee5\u53ca\u5728\u63a8\u8fdb\u7f55\u89c1\u75c5\u9632\u6cbb\u4e8b\u4e1a\u548c\u63a8\u884c\u5168\u6c11\u5065\u5eb7\u56fd\u5bb6\u6218\u7565\u76ee\u6807\u4e0a\u7684\u51b3\u5fc3\u3002\u827e\u6ee1\u6b23<sup>&reg;<\/sup>\u901a\u8fc7\u4f18\u5148\u5ba1\u8bc4\u5ba1\u6279\u901a\u9053\u5728\u56fd\u5185\u52a0\u901f\u83b7\u6279\u4e0a\u5e02\uff0c\u5e76\u4e8e\u6b64\u6b21\u7eb3\u5165\u533b\u4fdd\uff0c\u6b63\u662f\u8fd9\u4e00\u51b3\u5fc3\u7684\u751f\u52a8\u8bc1\u660e\u3002<\/p>\n<p>\u4e3a\u54cd\u5e94\u56fd\u5bb6\u53f7\u53ec\uff0c\u7f57\u6c0f\u4e00\u76f4\u79ef\u6781\u901a\u8fc7\u5f00\u5c55\u6148\u5584\u63f4\u52a9\u3001\u53c2\u4e0e\u56fd\u5bb6\u533b\u4fdd\u8c08\u5224\u3001\u53c2\u4e0e\u62d3\u5c55\u57ce\u5e02\u60e0\u6c11\u4fdd\u7b49\u65b9\u5f0f\uff0c\u52a9\u529b\u7f55\u89c1\u75c5\u591a\u5c42\u6b21\u533b\u7597\u4fdd\u969c\u4f53\u7cfb\u7684\u5efa\u8bbe\u3002\u4e0e\u6b64\u540c\u65f6\uff0c\u7f57\u6c0f\u8fd8\u643a\u624b\u5404\u754c\u5f00\u5c55&quot;\u6491\u542f\u672a\u6765\u2014\u2014SMA\u8d85\u7ea7\u5988\u5988\u5168\u7ef4\u652f\u6491\u8ba1\u5212&quot;\u7b49\u7cfb\u5217\u75be\u75c5\u79d1\u666e\u4e0e\u4eba\u6587\u5173\u7231\u9879\u76ee\uff0c\u4ee5\u671f\u51dd\u805a\u66f4\u5e7f\u6cdb\u7684\u529b\u91cf\u4e3a\u60a3\u8005\u5bb6\u5ead\u6253\u9020\u96c6&quot;\u7b5b\u3001\u8bca\u3001\u6cbb\u3001\u4fdd&quot;\u4e00\u4f53\u5316\u3001\u5168\u65b9\u4f4d\u7684\u652f\u6301\u4f53\u7cfb\u3002<\/p>\n<p>SMA\u9886\u57df\u7684&quot;\u6377\u62a5\u9891\u4f20&quot;\uff0c\u662f\u7f57\u6c0f\u5728\u795e\u7ecf\u79d1\u5b66\u9886\u57df\u6df1\u8015\u7684\u7f29\u5f71\u3002\u9762\u5bf9\u8fd9\u4e00\u6700\u96be\u653b\u514b\u548c\u6cbb\u6108\u7684\u75be\u75c5\u9886\u57df\u4e4b\u4e00\uff0c\u7f57\u6c0f\u6b63\u52a0\u5927\u529b\u5ea6\u63a8\u8fdb\u4e0e\u62d3\u5c55\u76f8\u5173\u4ea7\u54c1\u7ba1\u7ebf\uff0c\u5411&quot;\u8ba9\u4eba\u7c7b\u4e0d\u518d\u53d7\u795e\u7ecf\u7cfb\u7edf\u75be\u75c5\u7684\u56f0\u6270\uff0c\u521b\u9020\u4e00\u4e2a\u795e\u7ecf\u7cfb\u7edf\u4e0d\u518d\u9650\u5236\u4eba\u7c7b\u6f5c\u80fd\u7684\u660e\u5929&quot;\u7684\u76ee\u6807\u8fc8\u8fdb\u3002<\/p>\n<div>\n<table border=\"1\" cellspacing=\"0\" cellpadding=\"0\" class=\"prnbcc\">\n<tbody>\n<tr>\n<td class=\"prnpr2 prnpl2 prnvab prnsbtb1 prnrbrb1 prnsbbb1 prnsblb1\" colspan=\"1\" rowspan=\"1\">\n<p class=\"prnml4\"><span class=\"prnews_span\"><sup>[1] <\/sup>\u738b\u6587\u4fcf, \u6bdb\u59d7\u59d7, \u9a6c\u9e23. &quot;\u810a\u9ad3\u6027\u808c\u840e\u7f29\u75c7\u60a3\u513f\u8425\u517b\u7ba1\u7406\u7814\u7a76\u8fdb\u5c55.&quot; \u4e34\u5e8a\u513f\u79d1\u6742\u5fd7 40.3 (2022): 235-240.<\/span><\/p>\n<p class=\"prnml4\"><span class=\"prnews_span\"><sup>[2]&nbsp;<\/sup>\u56fd\u5bb6\u7edf\u8ba1\u5c40. 2021\u5e74\u56fd\u6c11\u7ecf\u6d4e\u548c\u793e\u4f1a\u53d1\u5c55\u7edf\u8ba1\u516c\u62a5[EB\/OL\uff3d. http:\/\/www.stats.gov.cn\/tjsj\/zxfb\/202202\/t20220227_1827960.html, 2022-10-25.<\/span><\/p>\n<p class=\"prnml4\"><span class=\"prnews_span\"><sup>[3]&nbsp;<\/sup>\u810a\u9ad3\u6027\u808c\u840e\u7f29\u75c7\u591a\u5b66\u79d1\u7ba1\u7406\u4e13\u5bb6\u5171\u8bc6. \u4e2d\u534e\u533b\u5b66\u6742\u5fd7. 2019. 99(19): 1460-1467.<\/span><\/p>\n<p class=\"prnml4\"><span class=\"prnews_span\"><sup>[4]&nbsp;<\/sup>\u56fd\u5bb6\u536b\u751f\u5065\u5eb7\u59d4\u529e\u516c\u5385. \u7f55\u89c1\u75c5\u8bca\u7597\u6307\u5357\uff082019\u5e74\u7248\uff09[Z].2019-02-27<\/span><\/p>\n<p class=\"prnml4\"><span class=\"prnews_span\"><sup>[5]&nbsp;<\/sup>Baranello G, et al. N Engl J Med. 2021 Mar 11;384(10):915-923.<\/span><\/p>\n<\/td>\n<\/tr>\n<\/tbody>\n<\/table><\/div>\n<p>&nbsp;<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u4e0a\u6d772023\u5e741\u670819\u65e5 \/\u7f8e\u901a\u793e\/ &#8212; 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SMA\u9886\u57df\u7684&quot;\u6377\u62a5\u9891\u4f20&quot;\uff0c\u662f\u7f57\u6c0f\u5728\u795e\u7ecf\u79d1\u5b66\u9886\u57df\u6df1\u8015\u7684\u7f29\u5f71\u3002\u9762\u5bf9\u8fd9\u4e00\u6700\u96be\u653b\u514b\u548c\u6cbb\u6108\u7684\u75be\u75c5\u9886\u57df\u4e4b\u4e00\uff0c\u7f57\u6c0f\u6b63\u52a0\u5927\u529b\u5ea6\u63a8\u8fdb\u4e0e\u62d3\u5c55\u76f8\u5173\u4ea7\u54c1\u7ba1\u7ebf\uff0c\u5411&quot;\u8ba9\u4eba\u7c7b\u4e0d\u518d\u53d7\u795e\u7ecf\u7cfb\u7edf\u75be\u75c5\u7684\u56f0\u6270\uff0c\u521b\u9020\u4e00\u4e2a\u795e\u7ecf\u7cfb\u7edf\u4e0d\u518d\u9650\u5236\u4eba\u7c7b\u6f5c\u80fd\u7684\u660e\u5929&quot;\u7684\u76ee\u6807\u8fc8\u8fdb\u3002 [1] \u738b\u6587\u4fcf, \u6bdb\u59d7\u59d7, \u9a6c\u9e23. &quot;\u810a\u9ad3\u6027\u808c\u840e\u7f29\u75c7\u60a3\u513f\u8425\u517b\u7ba1\u7406\u7814\u7a76\u8fdb\u5c55.&quot; \u4e34\u5e8a\u513f\u79d1\u6742\u5fd7 40.3 (2022): 235-240. [2]&nbsp;\u56fd\u5bb6\u7edf\u8ba1\u5c40. 2021\u5e74\u56fd\u6c11\u7ecf\u6d4e\u548c\u793e\u4f1a\u53d1\u5c55\u7edf\u8ba1\u516c\u62a5[EB\/OL\uff3d. http:\/\/www.stats.gov.cn\/tjsj\/zxfb\/202202\/t20220227_1827960.html, 2022-10-25. [3]&nbsp;\u810a\u9ad3\u6027\u808c\u840e\u7f29\u75c7\u591a\u5b66\u79d1\u7ba1\u7406\u4e13\u5bb6\u5171\u8bc6. \u4e2d\u534e\u533b\u5b66\u6742\u5fd7. 2019. 99(19): 1460-1467. [4]&nbsp;\u56fd\u5bb6\u536b\u751f\u5065\u5eb7\u59d4\u529e\u516c\u5385. \u7f55\u89c1\u75c5\u8bca\u7597\u6307\u5357\uff082019\u5e74\u7248\uff09[Z].2019-02-27 [5]&nbsp;Baranello G, et al. N Engl J Med. 2021 Mar 11;384(10):915-923. &nbsp;&hellip; <a class=\"read-more\" href=\"https:\/\/www.xinwengao.com\/cn\/pr\/2023011823250088823\">Read More<\/a><\/p>\n","protected":false},"author":556,"featured_media":0,"comment_status":"close","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1965],"tags":[],"class_list":["post-88823","post","type-post","status-publish","format-standard","hentry","category-partnerships"],"amp_enabled":true,"_links":{"self":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/88823","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/users\/556"}],"replies":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/comments?post=88823"}],"version-history":[{"count":1,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/88823\/revisions"}],"predecessor-version":[{"id":88824,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/88823\/revisions\/88824"}],"wp:attachment":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/media?parent=88823"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/categories?post=88823"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/tags?post=88823"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}