{"id":43435,"date":"2021-09-07T11:00:00","date_gmt":"2021-09-07T04:00:00","guid":{"rendered":"https:\/\/www.xinwengao.com\/cn\/pr\/2021090711000043435"},"modified":"2021-09-07T21:41:07","modified_gmt":"2021-09-07T13:41:07","slug":"neuexcell-therapeutics-%e5%92%8c-spark-therapeutics-%e5%ae%a3%e5%b8%83%e8%be%be%e6%88%90%e7%a0%94%e7%a9%b6%e5%90%88%e4%bd%9c%e5%8d%8f%e8%ae%ae%ef%bc%8c%e4%b8%ba%e4%ba%a8%e5%bb%b7%e9%a1%bf%e8%88%9e","status":"publish","type":"post","link":"https:\/\/www.xinwengao.com\/cn\/pr\/2021090711000043435","title":{"rendered":"NeuExcell Therapeutics \u548c Spark Therapeutics \u5ba3\u5e03\u8fbe\u6210\u7814\u7a76\u5408\u4f5c\u534f\u8bae\uff0c\u4e3a\u4ea8\u5ef7\u987f\u821e\u8e48\u75c7\u5f00\u53d1\u65b0\u578b\u57fa\u56e0\u7597\u6cd5"},"content":{"rendered":"<table border=\"0\" cellspacing=\"10\" cellpadding=\"5\" align=\"right\">\n<tbody>\n<tr>\n<td><img decoding=\"async\" src=\"https:\/\/www.xinwengao.com\/cn\/wp-content\/uploads\/NeuExcell_Logo.jpg\" border=\"0\" alt=\"\" title=\"logo\" hspace=\"0\" vspace=\"0\" width=\"118\" \/><\/td>\n<\/tr>\n<\/tbody>\n<\/table>\n<ul type=\"disc\">\n<li>\u8be5\u5408\u4f5c\u65e8\u5728\u5229\u7528 NeuExcell \u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\uff0c\u4e3a\u4ea8\u5ef7\u987f\u821e\u8e48\u75c7\u60a3\u8005\u5f00\u53d1\u6709\u6548\u4e14\u5b89\u5168\u7684\u6cbb\u7597\u65b9\u6cd5\u3002<\/li>\n<li>Spark Therapeutic \u62e5\u6709\u5353\u8d8a\u7684\u7814\u53d1\u80fd\u529b\u548c\u4e13\u6709\u7684\u817a\u76f8\u5173\u75c5\u6bd2 (AAV) \u8f7d\u4f53\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\uff0c\u8fd9\u5c06\u63a8\u52a8\u8be5\u8ba1\u5212\u7684\u53d1\u5c55\u5e76\u514b\u670d\u75c5\u6bd2\u8f7d\u4f53\u7528\u4e8e\u57fa\u56e0\u6cbb\u7597\u7684\u969c\u788d\u548c\u6311\u6218\u3002<\/li>\n<li>NeuExcell \u5c06\u83b7\u5f97\u9ad8\u8fbe\u7ea6 1.9 \u4ebf\u7f8e\u5143\u7684\u9884\u4ed8\u6b3e\u3001\u8bb8\u53ef\u8d39\u3001\u7814\u53d1\u548c\u9500\u552e\u91cc\u7a0b\u7891\u4ed8\u6b3e\u4ee5\u53ca\u4ea7\u54c1\u7279\u8bb8\u6743\u4f7f\u7528\u8d39\u3002<\/li>\n<\/ul>\n<p><p>\u7f8e\u56fd\u5bbe\u5dde\u5dde\u5b66\u9662\u548c\u8d39\u57ce2021\u5e749\u67087\u65e5 \/\u7f8e\u901a\u793e\/ &#8212;&nbsp;NeuExcell Therapeutics \u548c&nbsp;\u7f57\u6c0f\u96c6\u56e2\u5b50\u516c\u53f8Spark Therapeutics \uff08RO\u3001ROG\uff1bOTCQX\uff1bRHHBY\uff09\uff0c\u4eca\u5929\u5ba3\u5e03\u4e86\u4e00\u9879\u57fa\u56e0\u6cbb\u7597\u5408\u4f5c\u534f\u8bae\uff0c\u65e8\u5728\u4e3a\u4ea8\u5ef7\u987f\u821e\u8e48\u75c7\uff08HD\uff09\u60a3\u8005\u5f00\u53d1\u4e00\u79cd\u5b89\u5168\u6709\u6548\u7684\u6cbb\u7597\u65b9\u6cd5\u3002<\/p>\n<p>\u6839\u636e\u534f\u8bae\u6761\u6b3e\uff0cSpark Therapeutics \u5c06\u83b7\u5f97 NeuExcell \u4e13\u6709\u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\u7684\u4f7f\u7528\u6743\u3002 NeuExcell \u7684\u7814\u53d1\u56e2\u961f\u5c06\u4e0e Spark Therapeutics \u5bc6\u5207\u5408\u4f5c\u4ee5\u63a8\u8fdb\u8be5\u8ba1\u5212\u3002&nbsp;\u6839\u636e\u671f\u6743\u8bb8\u53ef\uff0cNeuExcell \u5c06\u83b7\u5f97\u9ad8\u8fbe\u7ea6 1.9 \u4ebf\u7f8e\u5143\u7684\u9884\u4ed8\u6b3e\u3001\u8bb8\u53ef\u8d39\u3001\u7814\u53d1\u548c\u9500\u552e\u91cc\u7a0b\u7891\u4ed8\u6b3e\u4ee5\u53ca\u4ea7\u54c1\u7279\u8bb8\u6743\u4f7f\u7528\u8d39\u3002&nbsp;\u6839\u636e\u672c\u534f\u8bae\uff0cSpark Therapeutics \u4eab\u6709NeuExcell \u7684&nbsp;HD \u8ba1\u5212\u7684\u5168\u7403\u72ec\u5bb6\u6388\u6743\u8bb8\u53ef\u3002<\/p>\n<p>NeuExcell Therapeutics \u9996\u5e2d\u6267\u884c\u5b98&nbsp;Ronald Lorijn \u8bf4\uff1a\u201c\u6211\u4eec\u5f88\u9ad8\u5174\u4e0e Spark Therapeutics \u5408\u4f5c\u3002&nbsp;\u4ed6\u4eec\u62e5\u6709\u5f00\u53d1\u57fa\u56e0\u7597\u6cd5\u7684\u4e13\u4e1a\u77e5\u8bc6\u548c\u80fd\u529b\uff0c\u8fd9\u4e9b\u7597\u6cd5\u53ef\u80fd\u6709\u51cf\u7f13\u3001\u963b\u6b62\u6216\u6cbb\u6108\u795e\u7ecf\u7cfb\u7edf\u75be\u75c5\u7684\u6f5c\u529b\uff0c\u5e76\u81f4\u529b\u4e8e\u63d0\u9ad8 AAV \u5de5\u7a0b\u7684\u884c\u4e1a\u6807\u51c6\uff0c\u56e0\u800cSpark\u662f\u6211\u4eec\u7406\u60f3\u7684\u5408\u4f5c\u4f19\u4f34\u6765\u52a0\u901f\u63a8\u52a8 HD \u8ba1\u5212\u201d\u3002<\/p>\n<p>\u201cSpark Therapeutics \u4e00\u76f4\u5728\u4e3a\u60a3\u8005\u5bfb\u627e\u6709\u6f5c\u529b\u7684\u7a81\u7834\u6027\u7597\u6cd5\uff0c\u5305\u62ec\u4ea8\u5ef7\u987f\u821e\u8e48\u75c5\u60a3\u8005\uff0c\u6765\u6311\u6218\u96be\u4ee5\u907f\u514d\u7684\u9057\u4f20\u75be\u75c5\u3002&nbsp;\u6211\u4eec\u671f\u5f85\u4e0e NeuExcell \u5408\u4f5c\u5e76\u63a2\u7d22\u4ed6\u4eec\u72ec\u7279\u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\u3002\u201d Spark Therapeutics \u9996\u5e2d\u79d1\u5b66\u5b98 <span class=\"xn-person\">Federico Mingozzi<\/span> \u535a\u58eb\u8bf4\u3002<\/p>\n<p>\u65e2\u5f80\u666e\u904d\u8ba4\u4e3a\u54fa\u4e73\u52a8\u7269\u7684\u6210\u719f\u795e\u7ecf\u5143\u4e0d\u80fd\u88ab\u66ff\u6362\uff0c\u56e0\u6b64\u8111\u90e8\u75be\u75c5\u7684\u6cbb\u7597\u65b9\u6cd5\u5f80\u5f80\u4fa7\u91cd\u4e8e\u51cf\u7f13\u75be\u75c5\u7684\u8fdb\u5c55\u3002 NeuExcell Therapeutics \u53ef\u80fd\u5df2\u7ecf\u627e\u5230\u4e86\u518d\u751f\u795e\u7ecf\u7ec4\u7ec7\u7684\u65b0\u65b9\u6cd5\u3002&nbsp;\u8be5\u516c\u53f8\u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\u662f\u57fa\u4e8e\u8f6c\u5f55\u56e0\u5b50\u4ecb\u5bfc\u7684\u8f6c\u5206\u5316\u6280\u672f\u800c\u6784\u5efa\u3002&nbsp;\u8be5\u5e73\u53f0\u65e8\u5728\u5c06\u5185\u6e90\u6027\u80f6\u8d28\u7ec6\u80de\u539f\u4f4d\u76f4\u63a5\u8f6c\u5206\u5316\u4e3a\u529f\u80fd\u6027\u7684\u65b0\u795e\u7ecf\u5143\u3002\u8fd9\u4e9b\u80f6\u8d28\u7ec6\u80de\u56f4\u7ed5\u7740\u795e\u7ecf\u5143\uff0c\u5e76\u4e14\u5728\u795e\u7ecf\u5143\u53d7\u4f24\u6216\u6b7b\u4ea1\u540e\u901a\u5e38\u4f1a\u4ea7\u751f\u5e94\u6fc0\u53cd\u5e94\u3002&nbsp;\u867d\u7136\u795e\u7ecf\u5143\u4e0d\u80fd\u5206\u88c2\u81ea\u6211\u518d\u751f\uff0c\u4f46\u80f6\u8d28\u7ec6\u80de\u5728\u635f\u4f24\u90e8\u4f4d\u53ef\u4ee5\u5206\u88c2\u518d\u751f\uff0c\u56e0\u6b64\u662f\u4ea7\u751f\u65b0\u795e\u7ecf\u5143\u7684\u53ef\u6301\u7eed\u6765\u6e90\uff0c\u5e76\u4e14\u80fd\u591f\u4ea7\u751f\u5927\u91cf\u7684\u65b0\u795e\u7ecf\u5143\u4ece\u800c\u8fbe\u5230\u6709\u4e34\u5e8a\u610f\u4e49\u7684\u6cbb\u7597\u6548\u679c\u3002 NeuExcell \u6b63\u5728\u5f00\u53d1\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2 (AAV) \u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u7597\u6cd5\uff0c\u80fd\u591f\u5728\u795e\u7ecf\u53d8\u6027\u90e8\u4f4d\u539f\u4f4d\u518d\u751f\u529f\u80fd\u6027\u65b0\u795e\u7ecf\u5143\u3002<\/p>\n<p>\u201c\u4e3a\u4e86\u6253\u7834\u9057\u4f20\u75be\u75c5\u7ed9\u60a3\u8005\u548c\u5bb6\u5ead\u6240\u9020\u6210\u7684\u969c\u788d\uff0cSpark\u9700\u8981\u4e0e\u5fd7\u540c\u9053\u5408\u7684\u4f19\u4f34\u5408\u4f5c\uff0c\u5c06\u521b\u65b0\u6280\u672f\u4e0e\u6211\u4eec\u5148\u8fdb\u7684\u4e13\u6709 AAV \u8f7d\u4f53\u5e73\u53f0\u76f8\u7ed3\u5408\u201d\uff0cSpark Therapeutics \u7684\u9996\u5e2d\u5546\u52a1\u5b98Joseph La Barge\u8bf4\uff0c&nbsp;\u201c\u5229\u7528\u6211\u4eec\u5728\u57fa\u56e0\u6cbb\u7597\u5f00\u53d1\u65b9\u9762\u7684\u4e13\u4e1a\u77e5\u8bc6\u548c NeuExcell \u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\u548c\u80fd\u529b\uff0c\u6211\u4eec\u53ef\u4ee5\u5171\u540c\u52aa\u529b\uff0c\u4e3a\u4ea8\u5ef7\u987f\u75c5\u60a3\u8005\u63d0\u4f9b\u6709\u6f5c\u529b\u7684\u65b0\u578b\u57fa\u56e0\u7597\u6cd5\u3002\u201d<\/p>\n<p>Spark Therapeutic \u9488\u5bf9\u4e2d\u67a2\u795e\u7ecf\u7cfb\u7edf\u7684\u5148\u8fdb\u4e13\u6709 AAV \u8f7d\u4f53\u5e73\u53f0\u5bf9 HD \u7814\u53d1\u8ba1\u5212\u6709\u663e\u8457\u7684\u4f18\u52bf\u3002&nbsp;\u591a\u5e74\u6765\uff0cSpark Therapeutics \u4e00\u76f4\u5904\u4e8e\u57fa\u56e0\u6cbb\u7597\u7814\u7a76\u7684\u524d\u6cbf\uff0c\u5728\u8be5\u9886\u57df\u62e5\u6709\u5e7f\u6cdb\u7684\u77e5\u8bc6\u548c\u80fd\u529b\uff0c\u53ef\u7528\u4e8e\u63a8\u52a8 HD \u8ba1\u5212\u7684\u53d1\u5c55\u3002<\/p>\n<p>\u76f8\u5173\u94fe\u63a5 :<\/p>\n<p>http:\/\/www.neuexcell.com<\/p>\n<blockquote class=\"wp-embedded-content\" data-secret=\"YCdS7lgmwn\"><p><a href=\"https:\/\/neuexcell.com\/\">Home<\/a><\/p><\/blockquote>\n<p><iframe class=\"wp-embedded-content\" sandbox=\"allow-scripts\" security=\"restricted\" style=\"position: absolute; clip: rect(1px, 1px, 1px, 1px);\" title=\"&#8220;Home&#8221; &#8212; NeuExcell Therapeutics Inc\" src=\"https:\/\/neuexcell.com\/embed\/#?secret=YCdS7lgmwn\" data-secret=\"YCdS7lgmwn\" width=\"600\" height=\"338\" frameborder=\"0\" marginwidth=\"0\" marginheight=\"0\" scrolling=\"no\"><\/iframe><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u8be5\u5408\u4f5c\u65e8\u5728\u5229\u7528 NeuExcell \u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\uff0c\u4e3a\u4ea8\u5ef7\u987f\u821e\u8e48\u75c7\u60a3\u8005\u5f00\u53d1\u6709\u6548\u4e14\u5b89\u5168\u7684\u6cbb\u7597\u65b9\u6cd5\u3002 Spark Therapeutic \u62e5\u6709\u5353\u8d8a\u7684\u7814\u53d1\u80fd\u529b\u548c\u4e13\u6709\u7684\u817a\u76f8\u5173\u75c5\u6bd2 (AAV) \u8f7d\u4f53\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\uff0c\u8fd9\u5c06\u63a8\u52a8\u8be5\u8ba1\u5212\u7684\u53d1\u5c55\u5e76\u514b\u670d\u75c5\u6bd2\u8f7d\u4f53\u7528\u4e8e\u57fa\u56e0\u6cbb\u7597\u7684\u969c\u788d\u548c\u6311\u6218\u3002 NeuExcell \u5c06\u83b7\u5f97\u9ad8\u8fbe\u7ea6 1.9 \u4ebf\u7f8e\u5143\u7684\u9884\u4ed8\u6b3e\u3001\u8bb8\u53ef\u8d39\u3001\u7814\u53d1\u548c\u9500\u552e\u91cc\u7a0b\u7891\u4ed8\u6b3e\u4ee5\u53ca\u4ea7\u54c1\u7279\u8bb8\u6743\u4f7f\u7528\u8d39\u3002 \u7f8e\u56fd\u5bbe\u5dde\u5dde\u5b66\u9662\u548c\u8d39\u57ce2021\u5e749\u67087\u65e5 \/\u7f8e\u901a\u793e\/ &#8212;&nbsp;NeuExcell Therapeutics \u548c&nbsp;\u7f57\u6c0f\u96c6\u56e2\u5b50\u516c\u53f8Spark Therapeutics \uff08RO\u3001ROG\uff1bOTCQX\uff1bRHHBY\uff09\uff0c\u4eca\u5929\u5ba3\u5e03\u4e86\u4e00\u9879\u57fa\u56e0\u6cbb\u7597\u5408\u4f5c\u534f\u8bae\uff0c\u65e8\u5728\u4e3a\u4ea8\u5ef7\u987f\u821e\u8e48\u75c7\uff08HD\uff09\u60a3\u8005\u5f00\u53d1\u4e00\u79cd\u5b89\u5168\u6709\u6548\u7684\u6cbb\u7597\u65b9\u6cd5\u3002 \u6839\u636e\u534f\u8bae\u6761\u6b3e\uff0cSpark Therapeutics \u5c06\u83b7\u5f97 NeuExcell \u4e13\u6709\u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\u7684\u4f7f\u7528\u6743\u3002 NeuExcell \u7684\u7814\u53d1\u56e2\u961f\u5c06\u4e0e Spark Therapeutics \u5bc6\u5207\u5408\u4f5c\u4ee5\u63a8\u8fdb\u8be5\u8ba1\u5212\u3002&nbsp;\u6839\u636e\u671f\u6743\u8bb8\u53ef\uff0cNeuExcell \u5c06\u83b7\u5f97\u9ad8\u8fbe\u7ea6 1.9 \u4ebf\u7f8e\u5143\u7684\u9884\u4ed8\u6b3e\u3001\u8bb8\u53ef\u8d39\u3001\u7814\u53d1\u548c\u9500\u552e\u91cc\u7a0b\u7891\u4ed8\u6b3e\u4ee5\u53ca\u4ea7\u54c1\u7279\u8bb8\u6743\u4f7f\u7528\u8d39\u3002&nbsp;\u6839\u636e\u672c\u534f\u8bae\uff0cSpark Therapeutics \u4eab\u6709NeuExcell \u7684&nbsp;HD \u8ba1\u5212\u7684\u5168\u7403\u72ec\u5bb6\u6388\u6743\u8bb8\u53ef\u3002 NeuExcell Therapeutics \u9996\u5e2d\u6267\u884c\u5b98&nbsp;Ronald Lorijn \u8bf4\uff1a\u201c\u6211\u4eec\u5f88\u9ad8\u5174\u4e0e Spark Therapeutics \u5408\u4f5c\u3002&nbsp;\u4ed6\u4eec\u62e5\u6709\u5f00\u53d1\u57fa\u56e0\u7597\u6cd5\u7684\u4e13\u4e1a\u77e5\u8bc6\u548c\u80fd\u529b\uff0c\u8fd9\u4e9b\u7597\u6cd5\u53ef\u80fd\u6709\u51cf\u7f13\u3001\u963b\u6b62\u6216\u6cbb\u6108\u795e\u7ecf\u7cfb\u7edf\u75be\u75c5\u7684\u6f5c\u529b\uff0c\u5e76\u81f4\u529b\u4e8e\u63d0\u9ad8 AAV \u5de5\u7a0b\u7684\u884c\u4e1a\u6807\u51c6\uff0c\u56e0\u800cSpark\u662f\u6211\u4eec\u7406\u60f3\u7684\u5408\u4f5c\u4f19\u4f34\u6765\u52a0\u901f\u63a8\u52a8 HD \u8ba1\u5212\u201d\u3002 \u201cSpark Therapeutics \u4e00\u76f4\u5728\u4e3a\u60a3\u8005\u5bfb\u627e\u6709\u6f5c\u529b\u7684\u7a81\u7834\u6027\u7597\u6cd5\uff0c\u5305\u62ec\u4ea8\u5ef7\u987f\u821e\u8e48\u75c5\u60a3\u8005\uff0c\u6765\u6311\u6218\u96be\u4ee5\u907f\u514d\u7684\u9057\u4f20\u75be\u75c5\u3002&nbsp;\u6211\u4eec\u671f\u5f85\u4e0e NeuExcell \u5408\u4f5c\u5e76\u63a2\u7d22\u4ed6\u4eec\u72ec\u7279\u7684\u795e\u7ecf\u518d\u751f\u57fa\u56e0\u6cbb\u7597\u5e73\u53f0\u3002\u201d Spark Therapeutics&hellip; <a class=\"read-more\" href=\"https:\/\/www.xinwengao.com\/cn\/pr\/2021090711000043435\">Read More<\/a><\/p>\n","protected":false},"author":556,"featured_media":43438,"comment_status":"close","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1965],"tags":[],"class_list":["post-43435","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-partnerships"],"amp_enabled":true,"_links":{"self":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/43435","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/users\/556"}],"replies":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/comments?post=43435"}],"version-history":[{"count":1,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/43435\/revisions"}],"predecessor-version":[{"id":43437,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/43435\/revisions\/43437"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/media\/43438"}],"wp:attachment":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/media?parent=43435"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/categories?post=43435"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/tags?post=43435"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}