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\u52c3\u6797\u683c\u6bb7\u683c\u7ff0\u98ce\u9669\u57fa\u91d1\u4e9a\u6d32\u8463\u4e8b\u603b\u7ecf\u7406\u5f20\u5dcd\u6021\u535a\u58eb\u8868\u793a\uff1a\u201c\u52c3\u6797\u683c\u6bb7\u683c\u7ff0\u98ce\u9669\u57fa\u91d1\u81f4\u529b\u4e8e\u6295\u8d44\u5168\u65b0\u6cbb\u7597\u7406\u5ff5\u4ee5\u89e3\u51b3\u9ad8\u5ea6\u672a\u88ab\u6ee1\u8db3\u7684\u533b\u7597\u9700\u6c42\u3002\u6211\u4eec\u5f88\u9ad8\u5174\u770b\u5230 Nuevocor \u6b63\u5728\u5c1d\u8bd5\u4f7f\u7528\u4e00\u79cd\u975e\u5e38\u521b\u65b0\u4e14\u6781\u5177\u6311\u6218\u6027\u7684\u57fa\u56e0\u7597\u6cd5\u6765\u6cbb\u7597\u7531\u57fa\u56e0\u5bfc\u81f4\u7684\u6269\u5f20\u578b\u5fc3\u808c\u75c5\uff0c\u6211\u4eec\u5e0c\u671b\u8fd9\u4e9b\u6f5c\u5728\u7597\u6cd5\u80fd\u591f\u6539\u53d8\u75be\u75c5\u8fdb\u7a0b\uff0c\u5e76\u5ef6\u957f\u6269\u5f20\u578b\u5fc3\u808c\u75c5\u60a3\u8005\u7684\u751f\u547d\u3002\u201d \u65b0\u52a0\u5761\u79d1\u6280\u7814\u7a76\u5c40\uff08A*STAR \u7b80\u79f0\u201c\u65b0*\u79d1\u7814\u201d\uff09\u751f\u7269\u533b\u5b66\u7814\u7a76\u7406\u4e8b\u4f1a\uff08Biomedical Research Council\uff09\u52a9\u7406\u603b\u88c1\u9ec4\u5b66\u6656\u6559\u6388\u8868\u793a\uff1a\u201c\u65b0\u52a0\u5761\u957f\u671f\u81f4\u529b\u4e8e\u7814\u53d1\u6295\u8d44\uff0c\u63a8\u52a8\u5065\u5eb7\u6210\u679c\u8f6c\u5316\u548c\u7ecf\u6d4e\u589e\u957f\uff0c\u5e76\u6784\u5efa\u5f53\u5730\u751f\u7269\u6280\u672f\u521b\u65b0\u751f\u6001\u7cfb\u7edf\u3002\u6211\u4eec\u5f88\u81ea\u8c6a\u80fd\u591f\u4e3a\u6765\u81ea\u65b0*\u79d1\u7814\u7684\u521b\u4e1a\u4f01\u4e1a Nuevocor \u63d0\u4f9b\u652f\u6301\uff0c\u5c06\u5353\u8d8a\u7684\u79d1\u5b66\u4ece\u5b9e\u9a8c\u5ba4\u8f6c\u5316\u5230\u4e34\u5e8a\u9636\u6bb5\uff0c\u5e2e\u52a9\u4ed6\u4eec\u5bf9\u96be\u4ee5\u6cbb\u7597\u7684\u5fc3\u810f\u75c5\u5f00\u53d1\u66f4\u9ad8\u6548\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u4ece\u800c\u6539\u5584\u60a3\u8005\u7684\u6cbb\u7597\u6210\u679c\u3002\u201d Nuevocor \u603b\u90e8\u4f4d\u4e8e\u65b0\u52a0\u5761\uff0c\u662f\u4e00\u5bb6\u672a\u4e0a\u5e02\u4e34\u5e8a\u524d\u751f\u7269\u5236\u836f\u516c\u53f8\uff0c\u4e13\u6ce8\u4e8e\u5f00\u53d1\u7528\u4e8e\u6cbb\u7597\u9057\u4f20\u6027\u5fc3\u808c\u75c5\u7684\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u7684\u57fa\u56e0\u7597\u6cd5\u4ee5\u6ee1\u8db3\u5de8\u5927\u4e14\u672a\u88ab\u6ee1\u8db3\u7684\u4e34\u5e8a\u9700\u6c42\u3002Nuevocor \u7684\u4e3b\u8981\u9879\u76ee lamin A\/C\u6269\u5f20\u578b\u5fc3\u808c\u75c5\uff08LMNA&nbsp;DCM\uff09\u57fa\u56e0\u7597\u6cd5\u57fa\u4e8e\u6570\u5341\u5e74\u6765\u5bf9 LMNA \u76f8\u5173\u75be\u75c5\u7684\u57fa\u672c\u673a\u5236\u7684\u7814\u7a76\uff0c\u8fd9\u4e9b\u57fa\u672c\u673a\u5236\u7531\u6765\u81ea\u65b0*\u79d1\u7814\u7684\u79d1\u5b66\u8054\u5408\u521b\u59cb\u4eba Colin Stewart \u548c Brian Burke \u53d1\u73b0\u5e76\u53d1\u5c55\u3002\u5176\u4ed6\u8054\u5408\u79d1\u5b66\u521b\u59cb\u4eba\u5305\u62ec\u6765\u81ea\u65af\u5766\u798f\u5927\u5b66\uff08Stanford University\uff09\u7684 AAV&hellip; <a class=\"read-more\" href=\"https:\/\/www.xinwengao.com\/cn\/pr\/2021061808000034472\">Read More<\/a><\/p>\n","protected":false},"author":556,"featured_media":8278,"comment_status":"close","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1965],"tags":[],"class_list":["post-34472","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-partnerships"],"amp_enabled":true,"_links":{"self":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/34472","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/users\/556"}],"replies":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/comments?post=34472"}],"version-history":[{"count":1,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/34472\/revisions"}],"predecessor-version":[{"id":34473,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/posts\/34472\/revisions\/34473"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/media\/8278"}],"wp:attachment":[{"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/media?parent=34472"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/categories?post=34472"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.xinwengao.com\/cn\/wp-json\/wp\/v2\/tags?post=34472"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}